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Patients With Congenital Myasthenic Syndrome Will be Treated With Mesenchymal Stem Cell Exosome Solution

Patients With Congenital Myasthenic Syndrome Will be Treated With Mesenchymal Stem Cell Exosome Solution

Recruiting
18 years and older
All
Phase 1
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Overview

Patients with Congenital Myasthenic Syndrome will be treated with Mesenchymal Stem Cell Exosome solution.

Description

Single Arm non-controlled study. Patients are prospectively evaluated then treated. Outcomes are tracked after treatment.

Eligibility

Inclusion Criteria:

  • Patients will need a diagnosis of Congenital Myasthenic Syndrome by a licensed physician.
  • Patients must be able to provide informed consent, or have a guardian who does.
  • Patient must be able to travel to the site of treatment.

Exclusion Criteria:

  • Patients will be excluded from the trial if they are pregnant or have active cancer (malignancy) at the screening consultation.

Study details
    Congenital Myasthenic Syndrome

NCT07226726

The Foundation for Orthopaedics and Regenerative Medicine

1 February 2026

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