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Genetic Studies of Strabismus, Congenital Cranial Dysinnervation Disorders (CCDDs), and Their Associated Anomalies

Genetic Studies of Strabismus, Congenital Cranial Dysinnervation Disorders (CCDDs), and Their Associated Anomalies

Recruiting
1 years and older
All
Phase N/A

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Overview

The purpose of this study is to identify genes associated with impaired development and function of the cranial nerves and brainstem, which may result in misalignment of the eyes (strabismus) and related conditions.

Description

If left untreated or unrecognized, strabismus or misalignment of the eyes, can impair the development of normal vision and is recognized to be an inherited trait in some families. The Engle Lab has investigated the genetics of complex and common strabismus and eyelid movement disorders for over 10 years and the lab's interests have expanded to include Congenital Cranial Dysinnervation Disorders (CCDDs) which are neurological disorders affecting one or more of the 12 cranial nerves. Cranial nerves control bodily functions such as movement of the eyes, transmission of visual information, smell, facial sensation, facial expression, blinking, hearing, balance, taste, chewing and swallowing.

Based on genetic studies on individuals with eye movement and eyelid disorders, the lab learned that some individuals have additional ocular defects, vascular, limb and other abnormalities. In addition, in some families relatives who carry the gene mutation may manifest the familial syndrome by having only some additional features but NOT the oculomotility disorder. Therefore, to gain greater understanding of the spectrum of the disorders being investigated, we may also enroll individuals without eye movement or lid defects who have symptoms associated with mutations in congenital cranial dysinnervation disorder (CCDD) genes.

Eligibility

Inclusion Criteria:

  • The Engle Lab is very interested in enrolling individuals with congenital conditions related to eye movement, cranial nerve and brainstem-based dysfunction, often broadly referred to as congenital cranial dysinnervation disorders (CCDDs).

Exclusion Criteria:

  • Individuals with cranial nerve disorders associated with known disorders, such as Saethre-Chotzen associated with established genetic mutations, or acquired conditions including trauma, stroke, tumor or spinal cord injuries.

Study details
    Congenital Fibrosis of Extraocular Muscles
    Duane Retraction Syndrome
    Duane Radial Ray Syndrome
    Mobius Syndrome
    Brown Syndrome
    Marcus Gunn Syndrome
    Strabismus Congenital
    Horizontal Gaze Palsy
    Horizontal Gaze Palsy With Progressive Scoliosis
    Facial Palsy
    Facial Paresis
    Hereditary
    Congenital
    Third Nerve Palsy
    Fourth Nerve Palsy
    Sixth Nerve Palsy
    Synkinesis
    Ocular Motility Disorders
    Levator-Medial Rectus Synkinesis
    Athabaskan Brainstem Dysgenesis
    Tongue Paralysis
    Ninth Nerve Disorder
    Fifth Nerve Palsy
    Seventh Nerve Palsy
    Eleventh Nerve Disorder
    Twelfth Nerve Disorder
    Vagus Nerve Paralysis
    Moebius Sequence

NCT03059420

Boston Children's Hospital

27 January 2024

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