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Adult Spinal Muscular Atrophy (SMA) China Registry

Adult Spinal Muscular Atrophy (SMA) China Registry

Non Recruiting
18 years and older
All
Phase N/A

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Overview

The primary objective of the study is to describe the natural history and utilization of disease modifying therapy (DMT) among adult Chinese participants with SMA linked to chromosome 5q (5q-SMA).

Eligibility

Key Inclusion Criteria:

-Genetically confirmed 5q-SMA.

Key Exclusion Criteria:

-Other types of SMA (non 5q-SMA).

NOTE: Other protocol defined Inclusion/Exclusion criteria may apply

Study details
    Muscular Atrophy
    Spinal

NCT05618379

Biogen

20 August 2025

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